A non-pathogenic viral vector suitable for in vivo gene transfer. It remains episomal and integrates into the host genome only very rarely.

Advanced Therapy Medicinal Products (ATMPs):

Medicinal products for human use based on genes, tissues, or cells. They include gene therapies, somatic cell therapies, and biotechnologically processed tissue products.

Good Manufacturing Practice(GMP) :

Guidelines for quality assurance in production processes

Gene Therapy Medicinal Product( GTMP ), genetically modified therapeutic products:

The term is primarily used within the EU regulatory framework. GTMPs are a subgroup of ATMPs.

Lentiviral vectors infect both dividing and non-dividing cells and integrate into the cell’s genome.

English: Clustered Regularly Interspaced Short Palindromic Repeats(CRISPR), English:CRISPR-associatedprotein 9 (Cas9)